In Utero Therapy for Serious Genetic Disorders: Saving and Improving Children’s Lives

Early fetal therapies have the power to change everything for babies and families affected by alpha thalassemia major or lysosomal storage diseases. Hear about the identification and treatment processes; windows of opportunity; and exciting potential benefits, risks and ethical considerations. Our presenters, fetal surgeon Tippi MacKenzie, MD, and genetic counselor Billie Lianoglou, also provide valuable info on patient registries and current clinical trials.

Refer to Fetal Treatment Center

Created by

UCSF Pediatrics

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